Publication & Citation Trends
Publications
0 total
No publications found.
Research Topics
Virus-based gene therapy research
(22)
Lysosomal Storage Disorders Research
(13)
CRISPR and Genetic Engineering
(11)
Pancreatic function and diabetes
(9)
Retinal Development and Disorders
(8)
Affiliations
Universitat Autònoma de Barcelona
Children's Hospital of Philadelphia
Howard Hughes Medical Institute
Gene Therapy Laboratory
Centro de Investigación Biomédica en Red Diabetes y Enfermedades Metabólicas Asociadas