Denise E. Sabatino
0000-0002-6116-5453
Publication & Citation Trends
Publications
0 total
Altered cleavage of human factor VIII at the B-domain and acidic region 3 interface enhances expression after gene therapy in hemophilia A mice. OA
Cited by 3
Semantic Scholar
Coagulation Factor VIII Regulates von Willebrand Factor Homeostasis In Vivo.
Cited by 5
Semantic Scholar
Coagulation Factor VIII Enhances the Cleavage of Von Willebrand Factor By ADAMTS13 In Vivo OA
Cited by 0
Semantic Scholar
Second Generation Adeno-Associated Viral Vector Using a Novel Factor VIII Variant with Improved Secretion Achieves Higher Factor VIII Expression in Non-Human Primates
Cited by 0
Semantic Scholar
Sustained Factor VIII Activity Following Single Dose of Non-Viral Integrating Gene Therapy
Cited by 0
Semantic Scholar
Evaluating the state of the science for adeno-associated virus integration: An integrated perspective OA
Cited by 141
Semantic Scholar
Topics in AAV integration come frontand center at ASGCT AAV Integration Roundtable. OA
Cited by 5
Semantic Scholar
Challenges in estimating numbers of vectors integrated in gene-modified cells using DNA sequence information. OA
Cited by 12
Semantic Scholar
Research Topics
Virus-based gene therapy research
(51)
Hemophilia Treatment and Research
(40)
CAR-T cell therapy research
(19)
Platelet Disorders and Treatments
(15)
CRISPR and Genetic Engineering
(15)
Affiliations
National Institutes of Health
St. Jude Children's Research Hospital
Children's Hospital of Philadelphia
George Washington University
Hospital of the University of Pennsylvania