Publication & Citation Trends
Publications
0 total
Systemic administration of novel engineered AAV capsids facilitates enhanced transgene expression in the macaque CNS OA
Cited by 43
Semantic Scholar
Directed evolution of a family of AAV capsid variants enabling potent muscle-directed gene delivery across species. OA
Cited by 373
Semantic Scholar
Pro-myogenic small molecules revealed by a chemical screen on primary muscle stem cells OA
Cited by 0
Semantic Scholar
In Situ Modification of Tissue Stem and Progenitor Cell Genomes OA
Cited by 40
Semantic Scholar
Therapeutic Gene Editing in Muscles and Muscle Stem Cells OA
Cited by 3
Semantic Scholar
Improving Stem Cell-Based Therapy and Developing a Novel Gene Therapy Approach for Treating Duchenne Muscular Dystrophy (DMD)
Cited by 0
Semantic Scholar
Gene Editing For Duchenne Muscular Dystrophy: Promise and Challenges for Clinical Application OA
Cited by 0
Semantic Scholar
483. In Vivo DMD Gene Editing in Muscles and Muscle Stem Cells of Dystrophic Mice OA
Cited by 3
Semantic Scholar
A multifunctional AAV–CRISPR–Cas9 and its host response OA
Cited by 570
Semantic Scholar
Research Topics
Muscle Physiology and Disorders
(10)
CRISPR and Genetic Engineering
(9)
Virus-based gene therapy research
(7)
Pluripotent Stem Cells Research
(6)
RNA Interference and Gene Delivery
(3)
Affiliations
Broad Institute
Howard Hughes Medical Institute
Harvard University
Royan Institute
University of Tehran