Publication & Citation Trends
Publications
0 total
P.193 Phosphoryl guanidine-containing backbone modifications enhance exon skipping, dystrophin restoration and survival in a severe mouse model for DMD
Cited by 0
Semantic Scholar
Control of backbone chemistry and chirality boost oligonucleotide splice switching activity OA
Cited by 39
Semantic Scholar
Endogenous ADAR-mediated RNA editing in non-human primates using stereopure chemically modified oligonucleotides
Cited by 91
Semantic Scholar
Stereochemistry Enhances Potency, Efficacy, and Durability of Malat1 Antisense Oligonucleotides In Vitro and In Vivo in Multiple Species OA
Cited by 24
Semantic Scholar
Stereochemistry Enhances Potency and Duration of Effect of MALAT1 Antisense Oligonucleotides In Vivo in the Mouse
Cited by 0
Semantic Scholar
DMD CLINICAL THERAPIES II
Cited by 0
Semantic Scholar
JIP2 haploinsufficiency contributes to neurodevelopmental abnormalities in human pluripotent stem cell–derived neural progenitors and cortical neurons OA
Cited by 8
Semantic Scholar
Alternative SET/TAFI Promoters Regulate Embryonic Stem Cell Differentiation OA
Cited by 25
Semantic Scholar
Research Topics
CRISPR and Genetic Engineering
(14)
RNA Interference and Gene Delivery
(7)
RNA regulation and disease
(7)
Pluripotent Stem Cells Research
(6)
Epigenetics and DNA Methylation
(4)
Affiliations
University of Pittsburgh
Wave Life Sciences (United States)
Whitehead Institute for Biomedical Research
Massachusetts Institute of Technology