Publication & Citation Trends
Publications
0 total
No publications found.
Research Topics
Glycogen Storage Diseases and Myoclonus
(7)
Pediatric Hepatobiliary Diseases and Treatments
(6)
Lysosomal Storage Disorders Research
(5)
Virus-based gene therapy research
(4)
Genetics and Neurodevelopmental Disorders
(4)
Affiliations
Hôpital Necker-Enfants Malades
Inserm
Sandia National Laboratories California
Université Paris Cité
Université Paris-Saclay