Publication & Citation Trends
Most Cited Works
Publications
26 total
Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency PDF
Cited by 48
OpenAlex
Somatic HLA mutations expose the role of class I–mediated autoimmunity in aplastic anemia and its clonal complications PDF
Cited by 83
OpenAlex
Somatic HLA Mutations Expose the Role of Class I-Mediated Autoimmunity in Aplastic Anemia and its Clonal Complications. OA
Cited by 78
Semantic Scholar
Emergence of clonal hematopoiesis in the majority of patients with acquired aplastic anemia PDF
Cited by 110
OpenAlex
Clonal evolution and clinical significance of copy number neutral loss of heterozygosity of chromosome arm 6p in acquired aplastic anemia
Cited by 44
OpenAlex
Impaired Telomere Maintenance and Decreased Canonical WNT Signaling but Normal Ribosome Biogenesis in Induced Pluripotent Stem Cells from X-Linked Dyskeratosis Congenita Patients PDF
Cited by 37
OpenAlex
Research Topics
Virus-based gene therapy research
(14)
RNA Interference and Gene Delivery
(6)
CRISPR and Genetic Engineering
(6)
CAR-T cell therapy research
(6)
Acute Myeloid Leukemia Research
(5)
Frequent Co-Authors
Affiliations
City Of Hope National Medical Center
Children's Hospital of Philadelphia
Johns Hopkins University
Loma Linda University
Alameda Hospital